Biometrics Services: Accelerating Clinical Trials For Rare Diseases

Precision medicine requires fast access to patient data throughout a trial, which is crucial for Cambridge, Massachusetts-based Sarepta Therapeutics, which focuses on therapy development for Duchenne Muscular Dystrophy (DMD), a genetic disorder affecting children with urgent medical needs.

Duchenne studies are lengthy, collecting substantial patient data over time. Due to the vulnerability of the patient population, Sarepta needed to analyze data to assess treatment safety and efficacy swiftly. To manage these trials effectively, Sarepta partners with technology and service providers who comprehend the urgency and can meet their data demands to create standard, reusable libraries for case report forms and edit checks across trials to save time and reduce costs.

By utilizing a centralized Rave EDC URL, Sarepta is able to achieve greater efficiencies and standardization. The team also requires technology platforms that offer access to and review data from multiple sources in a centralized, precise, and clean format for data review, exploration, and visualization.

As urgent therapy demands increased for Sarepta, the company realized that they would need a solution capable of completing even faster data reviews. Find out how the company was able to regain control over its data assets while increasing its ability to conduct comprehensive oversight and review activities across all data sources for faster decision-making and time to analyze.